autologous CD34+ hematopoietic stem cells transduced with LentiGlobin BB305 lentiviral vector encoding the human BA-T87Q-globin gene

autologous CD34+ hematopoietic stem cells transduced with LentiGlobin BB305 lentiviral vector encoding the human BA-T87Q-globin gene
Trade Name
Orphan Indication B-thalassemia major and intermedia
USA Market Approval USA
USA Designation Date 2013-03-18 00:00:00
Sponsor bluebird bio, Inc.;60 Binney Street;Cambridge, Massachusetts, 02142