autologous CD34+ hematopoietic stem cells transduced with LentiGlobin BB305 lentiviral vector encoding the human BA-T87Q-globin gene | |
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Trade Name | |
Orphan Indication | B-thalassemia major and intermedia |
USA Market Approval | USA |
USA Designation Date | 2013-03-18 00:00:00 |
Sponsor | bluebird bio, Inc.;60 Binney Street;Cambridge, Massachusetts, 02142 |