synthetic double-stranded siRNA oligonucleotide directed against hydroxyacid oxidase 1 (HAO1) mRNA

synthetic double-stranded siRNA oligonucleotide directed against hydroxyacid oxidase 1 (HAO1) mRNA
Trade Name
Orphan Indication Primary Hyperoxaluria Type 1
USA Market Approval USA
USA Designation Date 2016-02-08 00:00:00
Sponsor Alnylam Pharmaceuticals, Inc.;300 Third Street;Cambridge, Massachusetts, 02142