Adeno-associated viral vector serotype 8 encoding the humanATP7Bgene under the control of the human alpha-1 antitrypsin promoter

Adeno-associated viral vector serotype 8 encoding the humanATP7Bgene under the control of the human alpha-1 antitrypsin promoter
Trade Name
Orphan Indication Wilson disease
EU Market Approval EU
EU Designation Date 2015-11-11 00:00:00
Sponsor Aligen Therapeutics S.L.