Adeno-associated viral vector serotype 8 encoding the humanATP7Bgene under the control of the human alpha-1 antitrypsin promoter | |
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Trade Name | |
Orphan Indication | Wilson disease |
EU Market Approval | EU |
EU Designation Date | 2015-11-11 00:00:00 |
Sponsor | Aligen Therapeutics S.L. |