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adeno-associated viral vector serotype 5 encoding a microRNA targeted to human huntingtin gene |
|---|---|
| Trade Name | |
| Orphan Indication | Huntington disease |
| USA Market Approval | USA |
| USA Designation Date | 2017-09-27 00:00:00 |
| Sponsor | uniQure Biopharma B.V.;113 Hartwell Avenue;Lexington, Massachusetts, 02421 |
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