Antisense oligonucleotide complementary to the exonic splicer enhancer sequence at intron 26 of the centrosomal protein 290 pre-mRNA

Antisense oligonucleotide complementary to the exonic splicer enhancer sequence at intron 26 of the centrosomal protein 290 pre-mRNA
Trade Name
Orphan Indication Leber congenital amaurosis
EU Market Approval EU
EU Designation Date 2016-04-28 00:00:00
Sponsor ProQR Therapeutics IV BV