Antisense oligonucleotide complementary to the exonic splicer enhancer sequence at intron 26 of the centrosomal protein 290 pre-mRNA | |
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Trade Name | |
Orphan Indication | Leber congenital amaurosis |
EU Market Approval | EU |
EU Designation Date | 2016-04-28 00:00:00 |
Sponsor | ProQR Therapeutics IV BV |