aden-associated virus vector serotype 9 expressing human a-L-iduronidase

aden-associated virus vector serotype 9 expressing human a-L-iduronidase
Trade Name
Orphan Indication Hurler syndrome
USA Market Approval USA
USA Designation Date 2015-09-29 00:00:00
Sponsor REGENXBIO, Inc.;9712 Medical Center Drive, Suite 100;Rockville, Maryland, 20850