 |
adeno-associated virus serotype 2/6 (rAAV2/6) vectors encoding zinc finger nucleases (ZFNs) and the human alpha-L-iduronidase (hIDUA) gene |
|---|---|
| Trade Name | |
| Orphan Indication | Hurler syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2017-01-09 00:00:00 |
| Sponsor | Sangamo Therapeutics, Inc.;Point Richmond Tech Center, 501 Canal Boulevard;Richmond, California, 94804 |
