pyridopyrimidinone SMN2 splicing modifier

pyridopyrimidinone SMN2 splicing modifier
Trade Name
Orphan Indication Spinal muscular atrophy
USA Market Approval USA
USA Designation Date 2017-01-04 00:00:00
Sponsor Hoffmann-La Roche, Inc.;c/o Genentech, Inc., 1 DNA Way;South San Francisco, California, 94080