Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

Become a Partner.

Country Product Indication Sponsor Date
1-Cyclopropyl-3-[3-(5-morpholin-4-ylmethyl-1H-benzoimidazol-2-yl)-1H-pyrazol-4-yl]-urea Acute myeloid leukemia Astex Therapeutics Ltd;436 Cambridge Science Park, CB4 0QA; November 12, 2009
Amifampridine phosphate Lambert-Eaton Myasthenic Syndrome Catalyst Pharmaceuticals, Inc.;355 Alhambra Circle, Suite 1250;Coral Gables, Florida, 33134 November 12, 2009
3,4-Diaminopyridine phosphate Lambert-Eaton Myasthenic Syndrome Catalyst Pharmaceutical Partners, Inc.;355 Alhambra Circle, Suite 1500;Coral Gables, FL, 33134 November 12, 2009
Hypothiocyanite and lactoferrin Cystic fibrosis Alaxia Biotechnologies Sante;3-11 Rue de la Perlerie, F- 69120 Vaulx-en-velin; November 5, 2009
Cyclic pyranopterin monophosphate (cPMP) Molybdenum cofactor deficiency type A (MoCD) Alexion Pharmaceuticals, Inc.;100 College Street;New Haven, Connecticut, 06510 November 5, 2009
Exon 44 specific phosphorothioate oligonucleotide Duchenne muscular dystrophy BioMarin Pharmaceutical, Inc.;105 Digital Drive;Novato, California, 94949 November 5, 2009
Varbulin Glioblastoma Myrexis, Inc.;305 Chipeta Way;Salt Lake City, Utah, 84108 November 5, 2009
Salmeterol xinafoate/fluticasone propionate Symptomatic exophthalmos associated with thyroid related eye disease Lithera, Inc.;9191 Towne Center Drive;San Diego, California, 92122 October 29, 2009
Diannexin Prevention of ischemia-reperfusion injury in solid organ transplants Astellas Pharma Global Development, Inc.;Three Parkway North;Deerfield, Illinois, 60015 October 28, 2009
Dasiprotimut-T Follicular lymphoma Biovest International, Inc.;324 S. Hyde Park Avenue;Tampa, Florida, 33606 October 28, 2009
Caprine hyperimmune serum against HIV lysate Amyotrophic lateral sclerosis Daval International Limited;50 Lady Somerset Road; October 28, 2009
S-[2,3-bispalmitoyloxy-(2R)-propyl]-cysteinly-GNNDESNISFKEK Pancreatic Cancer MBiotec GmBH;Hohenweg 13, D-82229 Seefeld; October 20, 2009
Bevacizumab Melanoma stages IIb through IV as part of a combination chemotherapy regimen Genentech, Inc.;1 DNA Way;South San Francisco, California, 94080 October 13, 2009
4-benzyl-2-(a-naphtyl)-1,2,4-thiadiazolidine-3,5-dione Progressive supranuclear palsy NOSCIRA, S.A.;Avda. de la Industria, 52;Madrid October 13, 2009
Recombinant fusion protein-extracellular portion of CD95 fused to the Fc part of human IgG1 Glioblastoma Apogenix GmbH;Im Meuenheimer Feld 584; October 13, 2009
(S)-ethyl 2-amino-3-(4-(2-amino-6-((R)-1-(4-chloro-2-(3-methyl-1H-pyrazol-1-yl)phenyl)-2,2,2-trifluoroethoxy)pyrimidin-4-yl)phenyl)propanoate Carcinoid syndrome Ipsen Pharma October 8, 2009
Paclitaxel protein-bound particles for injection suspension Metastatic Melanoma Celgene Corporation;400 Connell Drive, Suite 7000;Berkeley Heights, New Jersey, 07922 October 1, 2009
L-pyr-L-glu-L-gln-L-leu-L-glu-L-arg-L-ala-L-leu-L-asn-L-ser-L-ser Prevention of delayed graft function following renal transplant Araim Pharmaceuticals, Inc.;712 Kitchawan Road;Ossining, New York, 10562 September 18, 2009
R-1-[2,3-dihydro-2-oxo-1-pivaloylmethyl-5-(2-pyridyl)-1 H -1,4-benzodiazepine -3-yl]-3-(3-methylaminophenyl)urea Gastric carcinoids Trio Medicines Ltd.;Pavillion View, Brighton BN1 1EY; September 10, 2009
Nucleic acid aptamer binding to tumor cell nucleolin Acute myeloid leukemia Antisoma, Inc.;300 Technology Square;Cambridge, Massachusetts, 02139 September 10, 2009
Cethromycin Prophylactic treatment of tularemia due to Francisella tularensis Advanced Life Sciences, Inc.;1440 Davey Road;Woodridge, Illinois, 60517 September 9, 2009
Cethromycin Prophylactic treatment of plague due to Yersinia pestis Advanced Life Sciences, Inc.;1440 Davey Road;Woodridge, Illinois, 60517 September 9, 2009
Belinostat T-cell lymphoma Spectrum Pharmaceuticals, Inc.;157 Technology Drive;Irvine, California, 92618 September 3, 2009
4-[4-[[[[3-(1,1-dimethylethyl)-1-(6-quinolinyl)-1H-pyrazol-5-yl]amino]carbonyl]-amino]-3-fluorophenoxyl]-N-methyl-2-pyridinecarboxamide, p-toluenesulfonate salt Chronic myeloid leukemia Deciphera Pharmaceuticals, LLC;643 Massachusetts, Suite 200;Lawrence, Kansas, 66044 September 3, 2009
Rigosertib Myelodysplastic syndromes Onconova Therapeutics, Inc.;375 Pheasant Run;Newtown, Pennsylvania, 18940 September 3, 2009