Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

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Country Product Indication Sponsor Date
Pergolide Tourette syndrome Sallee, Floyd R. M.D., Ph.D.;Cincinnati Children's Hospital Medical Center, 3333 Burnet Ave.;Cincinnati, Ohio, 45229 November 20, 1997
Calcium gluconate For use as a wash for hydrofluoric acid spills on human skin Calgonate Corp.;3310 South Ocean Blvd, Unit 132;Highland Beach, Florida, 33487 November 20, 1997
Pegylated recombinant human megakaryocyte growth and development factor For reducing the period of thrombocytopenia in patients undergoing hematopoietic stem cell transplantation Amgen, Inc.;One Amgen Center Dr.;Thousand Oaks, California, 91320 October 20, 1997
Apomorphine For use as rescue treatment for early morning motor dysfunction in late-stage Parkinson's disease Scherer DDS;Frankland Road, Swindon SN5 8RU;Wiltshire October 20, 1997
Recombinant human interleukin-12 Renal cancer Genetics Institute, Inc.;87 Cambridge Park Drive;Cambridge, Massachusetts, 02140 October 20, 1997
Alemtuzumab Chronic lymphocytic leukemia Genzyme Corporation;4545 Horizon Hill Blvd.;San Antonio, Texas, 78229 October 20, 1997
Recombinant human thrombopoietin For use in accelerating platelet recovery in patients undergoing hematopoietic stem cell transplantation Genentech, Inc.;1 DNA Way;South San Francisco, California, 94080 September 29, 1997
Purified extract of Pseudomonas aeruginosa Immune thrombocytopenia Able Laboratories, Inc.;200 Highland Avenue, Suite 30;Needham, Massachusetts, 02494 September 22, 1997
Testosterone For use as physiologic testosterone replacement in androgen deficient HIV+ patients with an associated weight loss Watson Laboratories;Research Park, 417 Wakara Way;Salt Lake City, Utah, 84108 September 22, 1997
Cysteamine hydrochloride Corneal cystine crystal accumulation in cystinosis patients Leadiant Biosciences, Inc.;9841 Washingtonian Blvd, Suite 500;Gaithersburg, Maryland, 20878 August 19, 1997
Recombinant human acid alpha-glucosidase; alglucosidase alfa Glycogen storage disease type II Genzyme Corporation;500 Kendall Street;Cambridge, Massachusetts, 02142 August 19, 1997
Alpha-melanocyte stimulating hormone Prevention and treatment of intrinsic acute renal failure due to ischemia National Institute of Diabetes, and Digestive and Kidney Diseases;National Institutes of Health, 31 Center Drive MSC, Building 31, Room 9N-222;Bethesda, Maryland, 20892 August 19, 1997
Short chain fatty acid enema Chronic radiation proctitis Richard I. Breuer, M.D.;1000 Central Street, Suite 615;Evanston, Illinois, 60201 August 19, 1997
Poloxamer 188 Vasospasm in subarachnoid hemorrhage patients following surgical repair of a ruptured cerebral aneurysm CytRx Corporation;154 Technology Parkway;Norcross, Georgia, 30092 August 5, 1997
Icodextrin 7.5% with Electrolytes Peritoneal Dialysis Solution Those patients having end stage renal disease and requiring peritoneal dialysis treatment Baxter Healthcare Corporation;Renal Division, 1620 Waukegan Road;McGaw Park, Illinois, 60085 July 18, 1997
Pentasaccharide ethyl glycoside consisting of one alpha-D-sialylosyl residue as a sodium salt, two beta-D-galactopyranosyl residues, one 2-acetamido-beta-D-glucopyranosyl unit, and one alpha-L-fucopyranosyl unit Neonates and infants undergoing cardiopulmonary bypass during surgical repair of congenital heart lesions Cytel Corporation;3525 John Hopkins Court;San Diego, California, 92121 July 18, 1997
Allogeneic human retinal pigment epithelial cells on gelatin microcarriers Hoehn and Yahr stage 3 and 4 Parkinson's disease Bayer Healthcare Pharmaceuticals, Inc.;100 Bayer Boulevard;Whippany, New Jersey, 07981 July 18, 1997
Busulfan Primary brain malignancies SuperGen, Inc.;Two Annabel Lane, Suite 220;San Ramon, California, 94583 July 7, 1997
Pegvisomant Acromegaly Sensus Corporation;Suite 430,, 98 San Jacinto Boulevard;Austin, Texas, 78701 June 24, 1997
Porcine Sertoli cells aseptically prepared for intracerebral co-implantation with fetal neural tissue Hoehn and Yahr stage four and five Parkinson's disease Titan Pharmaceuticals, Inc.;Post Office Plaza, 50 Division Street, Suite 503;Somerville, New Jersey, 08876 June 24, 1997
Allogeneic peripheral blood mononuclear cells sensitized against patient alloantigens by mixed lymphocyte culture Pancreatic Cancer Applied Immunotherapeutics, LLC;14132 E. Firestone Boulevard;Santa Fe Springs, California, 90670 June 13, 1997
Fampridine Chronic, incomplete spinal cord injury Acorda Therapeutics, Inc.;15 Skyline Dr.;Hawthorne, New York, 10532 June 2, 1997
Suramin Hormone-refractory prostate cancer Warner-Lambert Company;Parke-Davis Pharmaceutical Research Division, 2800 Plymouth Road;Ann Arbor, Michigan, 48105 May 6, 1997
Retroviral vector, R-GC and GC gene 1750 Gaucher disease Genzyme Corporation;500 Kendall Street;Cambridge, Massachusetts, 01701 May 6, 1997
Oxandrolone Patients with Duchenne's muscular dystrophy and Becker's muscular dystrophy Savient Pharmaceuticals, Inc.;One Tower Center Boulevard, 12th floor;East Brunswick, New Jersey, 08816 April 22, 1997