With an infrastructure in place to market its lone commercial product Ruconest, it made sense in 2019 for Pharming Group to scoop up another rare disease candidate in the same arena. Four years later, Pharming’s $20 million purchase of leniolisib from Novartis is set to bear dividends. On Friday, the...
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Mumbai – A 38-year-old woman who fell off a train last week thought she was lucky to have survived the accident despite suffering severe head and neck injuries. Shalini had reasons to think so as her CT scan came out normal. However, little did she know that her injury would...
LANSING, Mich. (WLNS) – on May 31 people strapped on their skates to raise money for a good cause. Chelsea Paradise was diagnosed with Huntington’s Disease 2 years ago. It’s a rare disease that destroys nerve cells in the brain, which can slow down someone’s thinking skills, and make it...
Jessica Kath has no pulse. But the 21-year old is full of heart, as her doctors have witnessed. “It’s been incredible watching her be a survivor,” says UT Southwestern cardiologist Mark Drazner. “Her story is amazing.” At birth, Jessica was diagnosed with a rare disease called Diamond-Blackfan Anemia. She doesn’t...
New York, NY. Women with atrial fibrillation (AF) undergoing a procedure called pulsed field ablation (PFA) have just as good outcomes as men with AF undergoing the same procedure, according to a large-scale international study led by the Icahn School of Medicine at Mount Sinai. This study is the first...
TORONTO, March 8, 2024 – Using large-scale U.S. data following patients for more than a decade, York University Faculty of Health researchers found that women with both metabolic syndrome and high-risk strains of human papillomavirus (HPV) are at a 2.6 times higher risk for mortality than women without either condition,...
PARIS, France – The multidisciplinary European consortium MARVAX will receive 7.4 million euros over the next four years for the research and development of vaccines against Marburg viruses. Researchers from France, Spain and Germany will develop novel vaccine candidates, which will be tested in preclinical animal models and bring them...
Shangai, China and TEL AVIV, Israel and ATHENS, Greece and ZURICH, Switzerland — The World Orphan Drug Alliance (WODA), a global alliance of commercial distributors dedicated to providing access to treatments for rare diseases and specialty medicines in complex markets around the world, has expanded its reach to include the...
The Cayman Islands joins the United Nations in observing the first annual Sickle Cell Disease World Day on Friday, 19 June. The worldwide event will raise awareness of the disease, and follows a United Nations General Assembly resolution adopted in December 2008 that recognizes sickle cell disease as a public...
Melbourne, Australia – Researchers at St Vincent’s Institute of Medical Research (SVI) in Melbourne have shown that a commonly prescribed rheumatoid arthritis drug can suppress the progression of type 1 diabetes. The world-first human trial, published today in the New England Journal of Medicine and led by SVI’s Professor Thomas...