Latest News

Stanford, Calif. – An “anti-hunger” molecule produced after vigorous exercise is responsible for the moderate weight loss caused by the diabetes medication metformin, according to a new study in mice and humans. The molecule, lac-phe, was discovered by Stanford Medicine researchers in 2022. The finding, made jointly by researchers at...
DETROIT – Ryder Washington started kindergarten this year. The 5-year-old loves to dance, practice martial arts and is obsessed with the Statue of Liberty. A few months ago he was diagnosed with a rare disease which in most cases leads to leukemia. The child’s family is hoping someone will be able...
FORT LEE, N.J. — Mezzion Pharmaceuticals is a rare disease company conducting the confirmatory pivotal phase 3 clinical trial in Fontan subjects: The Fontan Udenafil Exercise Longitudinal Assessment Trial- 2, or FUEL-2 trial. The company is pleased to announce Dr. Rahul Rathod, a pediatric cardiology specialist and leader with over...
MIAMI, FL – February 15, 2024 – A study co-led by researchers at Miami Cancer Institute, part of Baptist Health South Florida, found that ablative stereotactic magnetic resonance (MR)-guided adaptive radiation therapy may improve local control (LC) and overall survival (OS) in patients with borderline resectable (BRPC) and locally advanced...
NEW YORK — Scientists at Weill Cornell Medical College have developed a new mouse model of Parkinson’s disease (PD) that successfully reproduces the impairments of movement and the degenerative brain changes that occur in the human disease. Their research, performed in collaboration with investigators at Columbia University Medical Center, appears...
Last week, the Michigan House passed (88-20) House Bill 4167, which would create a Rare Disease Advisory Council (RDAC) within Michigan’s Department of Health and Human Services (MDHHS). The council would be required to conduct research, identify priorities, and make policy recommendations regarding access, treatments, and services for rare diseases...
Bozeman, Mont. and Vancuver, BC — Microbion Corporation announced that the US Patent and Trademark Office (USPTO) issued United States Patent No. 11,464,749 to Microbion with claims to the use of Microbion’s proprietary pravibismane inhaled composition for treatment of pulmonary infections. The patent, entitled “Bismuth-thiol compositions and methods of use,”...