Padma Panniker considers herself lucky. Although she suffers from blurry vision and chronic pain, she can still move, and even drives herself around; something unusual when compared with many multiple sclerosis (MS) sufferers. “Some of them are wheelchair-bound and even lose the ability to speak because of the illness,” she...
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LncRNA DLGAP1-AS2 is overexpressed in patients with non-small cell lung cancer (NSCLC) and may promote cell proliferation by upregulating cyclin D1 by sponging miR-503, according to a study published in BMC Pulmonary Medicine. Effective targets for lung cancer remain lacking. However, it has been suggested that lncRNAs and miRNAs are promising...
Taking care of a newborn is no easy feat. From feeding to changing, a baby requires all of one’s attention. Now imagine if the feeding and changing were the easy part. What if when you touched your baby ever-so-slightly, you risked damaging him or her for life? That is precisely...
Everyone in this world has needs but not all people have the same needs. Tabia McKinzie wants to raise awareness for people who have what most would call “special needs.” This has been brought to the forefront for McKinzie because of her daughter, Nandi. Nandi has Turner syndrome, a rare...
SAN DIEGO — Locanabio, Inc., a genetic medicines company developing RNA-targeted therapeutics for patients with rare genetic neuromuscular and neurodegenerative diseases, announced that CureDuchenne Ventures, the strategic investment arm of CureDuchenne, has made an equity investment in Locanabio. This investment will support the development of the company’s snRNA-mediated exon skipping...
LEXINGTON, Mass. – LogicBio Therapeutics, Inc. (Nasdaq:LOGC), a clinical-stage genetic medicine company pioneering gene delivery and gene editing platforms to address rare and serious diseases from infancy through adulthood, today announced results from a retrospective study of the disease course in pediatric patients living with severe methylmalonic acidemia (MMA) caused...
LEXINGTON, Mass. – LogicBio Therapeutics, Inc. (Nasdaq:LOGC), a clinical-stage genetic medicine company pioneering gene delivery and gene editing platforms to address rare and serious diseases from infancy through adulthood, today announced an update on screening and enrollment activities for the SUNRISE Phase I/II clinical trial of LB-001, the company’s investigational treatment for...
LEXINGTON, Mass. – LogicBio Therapeutics, Inc. (Nasdaq:LOGC), a clinical-stage genetic medicine company pioneering gene editing and gene delivery platforms to address rare and serious diseases from infancy through adulthood, today announced that the first patient has been dosed with LB-001, the Company’s investigational single-administration gene editing therapy based on its proprietary...
LEXINGTON, Mass. – LogicBio Therapeutics, Inc. (Nasdaq:LOGC), a clinical-stage genetic medicine company pioneering gene delivery and gene editing platforms to address rare and serious diseases from infancy through adulthood, today announced the promotion of Daniel Gruskin, MD, as chief medical officer. Dr. Gruskin most recently served as senior vice president and head of clinical...
LEXINGTON – LogicBio Therapeutics, Inc. (Nasdaq: LOGC), a clinical-stage genetic medicine company, today provided an update on the LB-001 clinical development program. The U.S. Food and Drug Administration (FDA) has notified the company that its Phase 1/2 SUNRISE clinical trial of LB-001 in pediatric patients with methylmalonic acidemia (MMA) has...