Efficacy and Safety of Human Lipoprotein Lipase (LPL)[S447X] Expressed by an Adeno-Associated Viral Vector in LPL-deficient Subjects

Familial Lipoprotein Lipase Deficiency

Safety and Efficacy in LPL-Deficient Subjects of AMT-011, an Adeno-Associated Viral Vector Expressing Human Lipoprotein Lipase [S447X] Lipoprotein Lipase Enzyme Activity Assay Validation and Clinical Assessment Study to Re-assess and Re-confirm Data Previously Recorded About the Incidence and Severity of Acute Abdominal “Pancreatitis” Episodes in Lipoprotein Lipase Deficient (LPLD) Subjects Previously Enrolled on AMT Clinical Studies Efficacy and Safety of Human Lipoprotein Lipase (LPL)[S447X] Expressed by an Adeno-Associated Viral Vector in LPL-deficient Subjects Postprandial Fatty Acid Metabolism in Subjects With Lipoprotein Lipase Deficiency