Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA

Mucopolysaccharidosis Type IVA

A Study to Evaluate the Safety, Tolerability and Efficacy of BMN 110 in Subjects With Mucopolysaccharidosis IVA Efficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation A Study to Evaluate the Long-Term Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) Safety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome BMN 110 US Expanded Access Program Study of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome) A Double-Blind Study to Evaluate the Efficacy and Safety of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A Syndrome) Discovering New Biomarkers For Monitoring Disease Progression in Patients With Mucopolysaccharidosis IVA