Recombinant adeno-associated virus retinal pigment epithelium gene vector AAV2-hRPE65v2 | |
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Trade Name | |
Orphan Indication | Leber congenital amaurosis |
USA Market Approval | USA |
USA Designation Date | 2008-06-24 00:00:00 |
Sponsor | Spark Therapeutics, Inc.;3737 Market Street, Suite 1300;Philadelphia, Pennsylvania, 19104 |