adenovirus associated viral vector serotype 5 containing the human RPE65 gene | |
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Trade Name | |
Orphan Indication | Leber congenital amaurosis |
USA Market Approval | USA |
USA Designation Date | 2016-03-10 00:00:00 |
Sponsor | MeiraGTx Limited;450 East 29th Street, 15th Floor;New York, New York, 10016 |