|
Adeno-associated viral vector expressing human acid alpha glucosidase gene |
|---|---|
| Trade Name | |
| Orphan Indication | Pompe disease |
| USA Market Approval | USA |
| USA Designation Date | 2007-03-20 00:00:00 |
| Sponsor | Audentes Therapeutics, Inc.;101 Montgomery St., #2650;San Francisco, California, 94104 |
