Adeno-Associated Viral Vector Expressing Low-Density Lipoprotein Receptor | |
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Trade Name | |
Orphan Indication | Homozygous Familial Hypercholesterolemia |
USA Market Approval | USA |
USA Designation Date | 2012-01-31 00:00:00 |
Sponsor | ReGenX Biosciences LLC;750 17th Street, NW, Suite 1100;Washington, District of Columbia, 20006 |