|
Adeno-Associated Viral Vector Expressing Low-Density Lipoprotein Receptor |
|---|---|
| Trade Name | |
| Orphan Indication | Homozygous Familial Hypercholesterolemia |
| USA Market Approval | USA |
| USA Designation Date | 2012-01-31 00:00:00 |
| Sponsor | ReGenX Biosciences LLC;750 17th Street, NW, Suite 1100;Washington, District of Columbia, 20006 |
