pyridopyrimidinone SMN2 splicing modifier | |
---|---|
Trade Name | |
Orphan Indication | Spinal muscular atrophy |
USA Market Approval | USA |
USA Designation Date | 2017-01-04 00:00:00 |
Sponsor | Hoffmann-La Roche, Inc.;c/o Genentech, Inc., 1 DNA Way;South San Francisco, California, 94080 |
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