|
ataluren |
|---|---|
| Trade Name | Translarna |
| Orphan Indication | Hurler syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2014-12-10 00:00:00 |
| Sponsor | PTC Therapeutics, Inc.;100 Corporate Court;South Plainfield, New Jersey, 07080 |
|
ataluren |
|---|---|
| Trade Name | Translarna |
| Orphan Indication | Hurler syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2014-12-10 00:00:00 |
| Sponsor | PTC Therapeutics, Inc.;100 Corporate Court;South Plainfield, New Jersey, 07080 |