aden-associated virus vector serotype 9 expressing human a-L-iduronidase | |
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Trade Name | |
Orphan Indication | Hurler syndrome |
USA Market Approval | USA |
USA Designation Date | 2015-09-29 00:00:00 |
Sponsor | REGENXBIO, Inc.;9712 Medical Center Drive, Suite 100;Rockville, Maryland, 20850 |