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synthetic double-stranded (hybridized duplex) ribonucleic acid oligonucleotide specific to hydroxyacid oxidase 1 gene |
|---|---|
| Trade Name | |
| Orphan Indication | Primary Hyperoxaluria Type 1 |
| USA Market Approval | USA |
| USA Designation Date | 2015-04-22 00:00:00 |
| Sponsor | Dicerna Pharmaceuticals, Inc.;87 Cambridgepark Drive;Cambridge, Massachusetts, 02140 |
