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Page 6
Videos
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Dr. Birch: Understanding X-Linked Retinoschisis (XLRS)
440 views | 8 years ago
Shwachman-Diamond Syndrome : Jordyn’s SDS Journey
937 views | 9 years ago
Is Polio Still a Threat? – The Doctors
551 views | 9 years ago
Rett Syndrome : Burden of Disease Study
436 views | 9 years ago
Inspiring stories from our families – Rettsyndrome.org
437 views | 9 years ago
What is Ulcerative Colitis?
366 views | 9 years ago
Angelman Syndrome: Close to a cure?
580 views | 9 years ago
Hereditary Angioedema
615 views | 9 years ago
Nephrotic Syndrome 101 Webinar
451 views | 9 years ago
Ankar family profile
446 views | 9 years ago
Lysosomal Storage Diseases
518 views | 9 years ago
Alpha-1 Antitrypsin Deficiency – Not A Rare Disease, But Rarely Diagnosed
425 views | 9 years ago
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News
Chugai Launches “ELEVIDYS” as Japan’s First Regenerative Medical
UCLA Scientists Develop Nonviral Gene-Editing Therapy that Could Enabl
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BioVersys Reports Promising Phase 2a Results for Novel Tuberculosis Th
YolTech Therapeutics Announces Positive Interim Data on YOLT-202 for t
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