Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
2-[(R)-2-methylpyrrolidin-2-yl]-1H-benzimadazole-4-carboxamide Malignant melanoma stages IIb through IV AbbVie, Inc.;1 N. Waukegan Road;North Chicago, Illinois, 60064 December 18, 2007
Fludarabine phosphate oral tablets Chronic lymphocytic leukemia Sanofi-Aventis U.S., Inc.;55 Corproate Drive, P. O. Box 5925;Bridgewater, New Jersey, 08807 December 18, 2007
Chlorotoxin Glioma Morphotek, Inc.;210 Welsh Pool Road;Exon, Pennsylvania, 19341 December 18, 2007
Canakinumab Cryopyrin-associated periodic syndromes Novartis Pharmaceuticals Corporation;One Health Plaza;East Hanover, New Jersey, 07936 December 18, 2007
Elesclomol Metastatic Melanoma Synta Pharmaceuticals Corporation;45 Hartwell Ave.;Lexington, Massachusetts, 02421 December 18, 2007
Brivudin Pancreatic Cancer SciClone Pharmaceuticals, Inc.;901 Mariner's Island Blvd.;San Mateo, California, 94404 November 15, 2007
Metronidazole 10% ointment Topical treatment of active perianal Crohn's disease SLA Pharma (UK) Ltd;Elite House, Hill Farm Industrial Estate;Watford WD25 7SA November 8, 2007
Carlumab Idiopathic pulmonary fibrosis Janssen Biotech, Inc.;Welsh & McKean Roads, P.O. Box 776;Spring House, Pennsylvania, 19477 November 8, 2007
Betahistine dihydrochloride Prader-Willi syndrome Floyd R. Sallee, M.D., Ph.D.;University of Cincinnati School of Medicine, ML 0559;Cincinnati, Ohio, 45267 November 8, 2007
Human factor X Factor X deficiency Bio Products Laboratory;Dagger Lane, Hertfordshire, WD6 3BX; November 8, 2007
4,5 dibromorhodamine methyl ester Graft Versus Host Disease Kiadis Pharma Netherlands B.V.;Entrada 231 - 234; October 23, 2007
Eteplirsen Duchenne muscular dystrophy Sarepta Therapeutics, Inc.;215 First Street, Suite 415;Cambridge, Massachusetts, 02142 October 23, 2007
N-[4-(3-amino-1H-indazol-4-yl)phenyl]-N1-(2-fluoro-5-methylphenyl) urea Acute myeloid leukemia AbbVie, Inc.;1 N Waukegan Road, AP34/RA72;North Chicago, Illinois, 60064 October 23, 2007
N-adamantanyl-N’-Geranyl-ethylenediamine Tuberculosis Sequella, Inc.;9610 Medical Center Drive;Rockville, Maryland, 20850 October 16, 2007
Microvesiculated modified glycosylated tissue factor Non-life threatening, mild to severe bleeding episodes due to cutaneous injuries or dental procedures in patients with von Willebrand disease Thrombotargets Corp.;2530 Meridian Parkway;Durham, North Carolina, 27713 October 11, 2007
Interferon gamma Idiopathic pulmonary fibrosis mondoBIOTECH Laboratories AG;Herrengasse 21, 9490 Vaduz, Liechtenstein; October 11, 2007
Tamibarotene Acute promyelocytic leukemia CytRx Corporation;3030 Bunker Hill Road, Suite 101;San Diego, California, 92109 October 11, 2007
Dexpramipexole Amyotrophic lateral sclerosis Knopp Biosciences LLC;2100 Wharton Street, Suite 615;Pittsburgh, Pennsylvania, 15203 October 11, 2007
Recombinant human fibrinogen Bleeding in patients deficient in fibrinogen Pharming Technologies B.V.;Archimedesweg 4; October 4, 2007
Panobinostat Cutaneous T-cell lymphoma Novartis Pharmaceuticals Corporation;One Health Plaza;East Hanover, New Jersey, 07936 September 26, 2007
Colchicine Familial Mediterranean fever AR Holding Company, Inc.;1100 Orthodox Street;Philadelphia, Pennsylvania, 19124 September 25, 2007
Colchicine Behçet’s Disease AR Scientific, Inc.;1100 Orthodox Street;Philadelphia, Pennsylvania, 19124 September 25, 2007
5′-O-(trans-9′-octadecenoyl)-1-ß-D-arabinofuranosyl cytosine Acute myleoid leukaemia Aqualis ASA September 14, 2007
Pafuramidine maleate African trypanosomiasis Immtech Pharmaceuticals, Inc.;150 Fairway Drive;Vernon Hills, Illinois, 60061 August 31, 2007
Ascorbic acid Scurvy McGuff Pharmaceuticals Inc.;2921 W. MacArthur Blvd., Suite 141;Santa Ana, California, 92704 August 31, 2007