Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Levofloxacin Cystic fibrosis Horizon Pharma USA, Inc.;150 S. Saunders Road, Suite 100;Lake Forest, Illinois, 60045 February 27, 2008
Arylsulfatase A (rhASA) Metachromatic leukodystrophy Shire Human Genetic Therapies, Inc.;300 Shire Way;Lexington, Massachusetts, 02421 February 27, 2008
Belatacept Prophylaxis of organ rejection in renal allograft recipients Bristol-Myers Squibb Company;P. O. Box 4000;Princeton, New Jersey, 08543 February 20, 2008
Doxorubicin with pluronics F-127 and L-61 Stomach Cancer Supratek Pharma, Inc.;6100 Royalmount Avenue, Montreal;Quebec H4P 2R2 February 20, 2008
Cys-His-Ala-Val-Cys For use in conjunction with melphalen for the treatment of malignant melanoma, AJCC stages IIB, IIC, III and IV Adherex Technologies, Inc.;4620 Creekstone Drive;Durham, North Carolina, 27703 February 14, 2008
Everolimus Neuroendocrine tumors Novartis Pharmaceuticals Corporation;One Health Plaza, Build 337, A14.5D;East Hanover, New Jersey, 07936 February 14, 2008
(+/-)-cis-3-(4-hydroxyphenyl)-4-(4-methoxyphenyl)-3,4-dihydro-2H-cromen-7-ol Metastatic Melanoma Marshall Edwards, Inc.;11975 El Camino Real, Suite 101;San Diego, California, 92130 February 1, 2008
Type 1 native bovine skin collagen Systemic scleroderma arGentis Pharmaceuticals, LLC;20 South Dudley Street;Memphis, Tennessee, 38139 February 1, 2008
Human prothrombin complex concentrate Reversal of anticoagulation therapy in patients needing treatment of serious or life threatening bleeding and/or needing urgent surgery or invasive procedures Octapharma USA, Inc.;121 River Street, 12th Floor;Hoboken, New Jersey, 07030 February 1, 2008
Triheptanoin Glycogen storage disorder II (Pompe disease) Baylor Research Institute;3330 Live Oak Blvd;Dallas, Texas, 75204 February 1, 2008
Autologous olfactory neural progenitors Spinal cord injury patients with ASIA Impairment grades A, B, or C RhinoCyte, Inc.;201 E. Jefferson Street;Louisville, Kentucky, 40202 February 1, 2008
N-(2-amino-phenyl)-4-[(4-pyridin-3-yl-pyrimidin-2-ylamino)-methyl] benzamide dihydrobromide Acute myeloid leukemia Mirati Therapeutics, Inc.;9363 Towne Center Drive, Suite 200;San Diego, California, 92121 February 1, 2008
Carfilzomib Multiple myeloma Onyx Therapeutics, Inc.;249 East Grand Avenue;South San Francisco, California, 94080 January 18, 2008
IDUA-HIRMAb fusion protein Mucopolysaccharidosis Type 1 (MPS) ArmaGen Technologies, Inc.;914 Colorado Ave.;Santa Monica, California, 90401 January 10, 2008
(+/-)-cis-3-(4-hydroxyphenyl)-4-(4-methoxyphenyl)-3,4-dihydro-2H-cromen-7-ol Pancreatic Cancer Marshall Edwards, Inc.;11975 El Camino Real, Suite 101;San Diego, California, 92130 January 10, 2008
(+/-)-cis-3-(4-hydroxyphenyl)-4-(4-methoxyphenyl)-3,4-dihydro-2H-cromen-7-ol Bile duct cancer Marshall Edwards, Inc.;11975 El Camino Real, Suite 101;San Diego, California, 92130 January 10, 2008
Tiotropium bromide Cystic fibrosis Boehringer Ingelheim Pharmaceuticals, Inc.;P. O. Box 368, 900 Ridgebury Road;Ridgefield, Connecticut, 06877 January 8, 2008
Clonazepam Intranasal Spray Recurrent acute repetitive seizures Jazz Pharmaceuticals, Inc.;3180 Porter Drive;Palo Alto, California, 94304 December 19, 2007
(R)-4-(3-morpholin-4-yl-l-phenylsulfanylmenthyl-propylamino)-N-(4-{4-[2-(4-chlorophenyl)-5,5-dimethylcyclohex-l-enylmethyl]-piperazin-l-yl}-benzoyl)-3-trifluoromethanesulfonylbenzenesulfonamide bis-hydrochloride Chronic lymphocytic leukemia AbbVie, Inc.;1 N Waukegan Road, AP34/RA72;North Chicago, Illinois, 60064 December 19, 2007
Coccidioidin SD Skin Test Antigen Coccidioidomycosis Allermed Labortories, Inc.;7203 Convoy Court;San Diego, California, 92111 December 19, 2007
Alefacept For use as prophylaxis of rejection in patients receiving allogenic solid organ transplants Astellas Pharma Global Development, Inc.;Three Parkway North;Deerfield, Illinois, 60015 December 19, 2007
(R)-4-(3-morpholin-4-yl-1-phenylsulfanylmethyl-propylamino)-N-(4-{4-[2-(4-chlorophenyl)-5,5-dimethylcyclohex-1-enylmethyl]-piperazin-1-yl}-benzoyl)-3-trifluoromethanesulfonylbenzenesulfonamide bis-hydrochloride Small cell lung cancer AbbVie, Inc;1 North Waukegan Road, Dept. PA77, Bldg. AP30-1;North Chicago, Illinois, 60064 December 19, 2007
Hemoximer (pyridoxalated hemoglobin polyoxyethylene) Cardiogenic shock Apex Bioscience, Inc.;109 Conner Drive, `;Chapel Hill, North Carolina, 27514 December 18, 2007
2-[(R)-2-methylpyrrolidin-2-yl]-1H-benzimadazole-4-carboxamide Malignant melanoma stages IIb through IV AbbVie, Inc.;1 N. Waukegan Road;North Chicago, Illinois, 60064 December 18, 2007
Fludarabine phosphate oral tablets Chronic lymphocytic leukemia Sanofi-Aventis U.S., Inc.;55 Corproate Drive, P. O. Box 5925;Bridgewater, New Jersey, 08807 December 18, 2007