Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Bosutinib Chronic myeloid leukemia Wyeth Pharmaceuticals, Inc.;Subsidiary of Pfizer, Inc., Eastern Point Road;Groton, Connecticut, 06340 February 24, 2009
2-iminobiotin Perinatal asphyxia Neurophyxia B.V.;Onderwijsboulevard 219; February 24, 2009
Cyclosporine Graft Versus Host Disease Sigmoid Pharma Limited;Dublin City University; February 17, 2009
(1R,3R,4R,5S)-3-O-[2-O-benzoyl-3-O-(sodium(2S)-3-cyclohexyl-propanoate- Sickle cell anemia Pfizer, Inc.;500 Arcola Road;Collegeville, Pennsylvania, 19426 February 17, 2009
Civamide Postherpetic neuralgia Winston Laboratories, Inc.;100 Fairway Drive;Vernon Hills, Illinois, 60061 February 17, 2009
Cyclosporine Graft Versus Host Disease Sigmoid Pharma Limited;Dublin City University; February 17, 2009
Cholest-4-en-3-one, oxime Spinal muscular atrophy Genentech, Inc.;A Roche Group Member, 1 DNA Way;South San Francisco, California, 94080 February 17, 2009
(S)-4,5-dihydro-2[2-hydroxy-3-(3,6,9-trioxadecyloxy)phenyl]-4-methyl-4-thiaxolecarboxylic acid Chronic iron overload in patients with transfusion-dependent anemias Ferrokin BioSciences, Inc.;2729 Debbie Court;San Carlos, California, 94070 February 4, 2009
HPV-16 cancer therapeutic trojan peptide vaccine HPV-16 expressing head and neck squamous cell carcinoma Gliknik, Inc.;801 W. Baltimore Street;Baltimore, Maryland, 21201 January 12, 2009
[Lu-177]-DOTA-Tyr3-Octreotate Gastro-entero-pancreatic neuroendocrine tumors Advanced Accelerator Applications;20 rue Diesel, 01630 Saint Genis Pouilly; January 12, 2009
Autologous olfactory neural progenitors Amyotrophic lateral sclerosis RhinoCyte, Inc.;201 E. Jefferson Street;Louisville, Kentucky, 40202 December 31, 2008
2-(2-phenylvinyl)-4-[4-methylpiperazin-l-yl)]-6-(5-methyl-2H-pyrazol-3-yl-amino)-pyrimidine L(+) tartrate salt Multiple myeloma EntreMed, Inc.;Research Triangle Park Center, Suite 400;Durham, North Carolina, 27703 December 22, 2008
Tosedostat Acute myeloid leukemia CTI BioPharma Corporation;3101 Western Avenue, Suite 600;Seattle, Washington, 98121 December 10, 2008
RNA, [P-deoxy-P-(dimethylamino)] (2′,3′-dideoxy-2′,3′-imino-2′,3′-seco) (2’a?5′)(C-m5U-C-C-A-A-C-A-m5U-C-A-A-G-G-A-A-G-A-m5U-G-G-C-A-m5U-m5U-m5U-C-m5U-A-G), P-[4-[[2-[2-(2-hydroxyethoxy)ethoxy] ethoxy]carbonyl]-1-piperazinyl]-N,Ndimethylaminophosphonamidate Duchenne muscular dystrophy AVI BioPharma International Ltd December 3, 2008
N2′-Deacetyl-N2′-[4-methyl-4-(oxobutyldithio)-1-oxopentyl]-maytansine-chimerised anti-CD138 IgG4 Monoclonal Antibody Multiple myeloma Biotest AG December 3, 2008
Chlorotoxin Metastatic Melanoma Morphotek, Inc.;210 Welsh Pool Road;Exon, Pennsylvania, 19341 December 2, 2008
Anti-CD30 Fc engineered humanized monoclonal antibody Hodgkin’s disease Xencor, Inc.;111 W. Lemon Avenue;Monrovia, California, 91016 December 2, 2008
Dexamethasone phosphate Corneal graft rejection EyeGate Pharmaceuticals, Inc.;100 Beaver Street;Waltham, Massachusetts, 02453 December 2, 2008
R-4-amino-3-(4-chlorophenyl)butanoic acid Fragile X syndrome Clinical Research Associates, LLC;160 Fifth Avenue, 7th Floor;New York, New York, 10010 November 28, 2008
MAGE-A3 cancer therapeutic Trojan peptide vaccine Squamous cell carcinoma of head and neck Gliknik, Inc.;801 W. Baltimore Street, Suite 501A;Baltimore, Maryland, 21201 November 24, 2008
Antineoplaston A10, antineoplaston AS2-1 Gliomas Burzynski Research Institute, Inc.;9432 Old Katy Road;Houston, Texas, 77055 November 21, 2008
GNE Lipoplex Hereditary inclusion body myopathy-2 Gradalis, Inc.;2545 Golden Bear Drive;Carrollton, Texas, 75006 November 13, 2008
Liposomal gadodiamide Glioma MedGenesis Therapeutix, Inc.;730-730 View Street, Victoria, BC V8W 3Y7; November 12, 2008
4, 5 dibromorhodamine methyl ester Follicular lymphoma Kiadis Pharma Canada, Inc.;2525 Marie Curie; October 30, 2008
Itraconazole suspension Topical treatment of fungal otitis externa (otomycosis) Fairfield Clinical Trials, LLC;200 Steep Hill Road;Weston, Connecticut, 06883 October 30, 2008