Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
(1-methyl-2-nitro-1H-imidazole-5-yl)methyl N,N’-bis(2-broethyl) diamidophosphate Pancreatic Cancer EMD Serono;One Technology Place;Rockland, Massachusetts, 02370 June 5, 2013
Diazepam auto-injector Management of selected, refractory patients with epilepsy on stable regimens of antiepileptic drugs, who require intermittent use of diazepam to control bouts of increased seizure activity Meridian Medical Technologies-a Pfizer subsidiary;445 Eastern Point Road;Groton, Connecticut, 06340 May 30, 2013
Abatacept Type 1 diabetes mellitus patients with residual beta cell function Orban Biotech LLC;64 Aspinwall Avenue;Brookline, Massachusetts, 02446 May 30, 2013
HIRMAb-IDS Hunter Syndrome ArmaGen Technologies, Inc.;914 Colorado Avenue;Santa Monica, California, 90401 May 15, 2013
N-{3-[(2-{[4-(4-acetylpiperazin-l-yl)-2-methoxyphenyl]amino}-5-(trifluoromethyl)pyrimidin-4-yl)amino]phenyl}prop-2-enamide Non-small cell lung cancer and mutations in the epidermal growth factor receptor Clovis Oncology, Inc.;2525 28th Street, Suite 100;Boulder, CO, 80301 May 14, 2013
H-Tyr-Gly-Arg-Lys-Lys-Arg-Arg-Gln-Arg-Arg-Arg-alys-aleu-Ser-Ser-Ile-Glu-Ser-Asp-Val-OH Subarachnoid hemorrhage NoNO, Inc.;399 Bathurst Street, Toronto M5T 2S8;Ontario May 14, 2013
Rociletinib Non-small cell lung cancer Clovis Oncology, Inc.;5500 Flatiron Parkway, Suite 100;Boulder, Colorado, 80301 May 14, 2013
DCVAC OvCa Ovarian cancer SOTIOS a.s.;Jankovcova 1518/2, 170 00 Praha 7; May 14, 2013
2-[4-Methoxy-3-(2-m-tolyl-ethoxy)-benzoylamino]-indian-2-carboxylic acid Systemic scleroderma Sanofi U. S., Inc.;55 Corporate Drive;Bridgewater, New Jersey, 08807 May 14, 2013
3,5-diiodothyropropionic acid Allan-Herndon-Dudley syndrome Zarion Pharmaceuticals P/L;8 Grandview Grove, Sassafras 3787;Victoria May 14, 2013
Budesonide Ulcerative colitis Santarus, Inc.;3611 Valley Centre Drive, Suite 400;San Diego, California, 92130 May 6, 2013
Daratumumab Multiple myeloma Janssen Research & Development, LLC;920 Route 202 South;Raritan, NJ, 08869 May 6, 2013
Adeno associated viral vector serotype rh.10 carrying the human SGSH and SUMF1 cDNAs Mucopolysaccharidosis type IIIA (Sanfilippo type A syndrome) Lysogene;52 rue La Boetie;Paris May 6, 2013
Daratumumab Multiple myeloma Janssen Biotech, Inc.;920 Route 202 South, PO Box 300;Raritan, New Jersey, 08869 May 6, 2013
Duvelisib small lymphocytic lymphoma Infinity Pharmaceuticals;780 Memorial Drive;Cambridge, Massachusetts, 02139 April 15, 2013
(S)-3-(1-(9H-purin-6-ylamino)ethyl)-8-chloro-2-phenylisoquinolin-1(2H)-one Chronic lymphocytic leukemia and small lymphocytic lymphoma Infinity Pharmaceuticals;780 Memorial Drive;Cambridge, MA, 02139 April 15, 2013
Brentuximab vedotin Patients with peripheral T-cell lymphoma, not otherwise specified Seattle Genetics, Inc.;21823 30th Drive Southeast;Bothell, Washington, 98021 April 15, 2013
4-(6-(4-(piperazin-1-yl)phenyl_pyrazolo[1,5-a]pyrimidin-3-yl)quinoline hydrochloride Fibrodysplasia ossificans progressiva La Jolla Pharmaceutical Company, Inc.;10182 Telesis Court, Suite 600;San Diego, California, 92121 April 15, 2013
Daunorubicin citrate liposome Acute myeloid leukemia Galen Limited;Seagoe Industrial Estate, Graigavon, BT63 5UA; April 15, 2013
Anti-inhibitor coagulant complex Hemophilia A Baxalta US, Inc.;One Baxter Way;West Lake Village, California, 91362 April 12, 2013
Cerliponase alfa Neuronal ceroid lipofuscinosis type 2 BioMarin Pharmaceutical, Inc.;105 Digital Drive;Novato, California, 94949 April 1, 2013
Kre-Celazine Juvenile rheumatoid arthritis joint and related tissue inflammation in the pediatric population All American Pharmaceutical & Natural Foods Corpor;2376 Main Street;Billings, Montana, 59105 April 1, 2013
Acamprosate Fragile X syndrome Confluence Pharmaceuticals, LLC;Box 528, 351 West 10th Street;Indianapolis, Indiana, 46202 March 25, 2013
N-tert-butyl-3-[(5-methyl-2-{[4-(2-pyrrolidin-1-ylethoxy)phenyl]amino}pyrimidin-4-yl)amino] benzenesulfonamide dihydrochloride monohydrate Polycythemia vera Impact Biomedicines;12526 High Bluff Drive, Suite 260;San Diego, California, 92130 March 21, 2013
Cell based therapeutic composed of allogeneic donor apoptotic cells Graft Versus Host Disease Enlivex Therapeutics Ltd.;POB 12167, Hadassah Ein Kerem;Jerusalem March 18, 2013