Treatments

The following database contains products that have been granted orphan status, or have been market approval in the EU or the USA.

You can filter the content by clicking on the titles: Product, Indication, Sponsor and Date. Clicking once, will filter the column alphabetically from A – Z and a second click on the same title will filter from Z – A.

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Country Product Indication Sponsor Date
Lestaurtinib Acute myeloid leukemia Teva Branded Pharmaceutical Products R&D;, Inc.;41 Moores Road, P. O. Box 4011;Frazer, Pennsylvania, 19355 March 24, 2006
N-[4-(4-amino-2-ethyl-lH-imidazo[4,5-c]quinolin-1-yl)butyl]methanesulfonamide Cutaneous T-cell lymphoma Pfizer, Inc.;50 Pequot Avenue, 6025-A3106;New London, Connecticut, 06320 March 24, 2006
Ethanol gel Congenital lymphatic malformations Orfagen;CRDPF - LANGLADE, 31035 Toulouse Cedex; March 13, 2006
Human umbilical tissue-derived cells Retinitis pigmentosa Janssen Research and Development, LLC;1400 McKean Road, P. O. Box 776;Spring House, Pennsylvania, 19477 March 13, 2006
Tissue repair cells obtained from autologous bone marrow expanded ex vivo with a cell production system Osteonecrosis Aastrom Biosciences, Inc.;Domino's Farms, Lobby K, 24 Frank Lloyd Wright Drive;Ann Arbor, Michigan, 48105 March 13, 2006
Clotrimazole Huntington disease EnVivo Pharmaceuticals, Inc.;480 Arsenal Street;Watertown, Massachusetts, 02472 March 13, 2006
Thymalfasin Metastatic Melanoma SciClone Pharmaceuticals, Inc.;950 Tower Lane, Suite 900;Foster City, California, 94404 March 13, 2006
Amikacin Bronchopulmonary Pseudomonas aeruginosa infections in cystic fibrosis patients Insmed, Inc.;Princeton Corporate Plaza, 9 Deer Park Drive, Suite C;Monmouth Junction, NJ, 08852-1923 March 9, 2006
Liposomal amikacin Cystic fibrosis Insmed, Inc.;Princeton Corporate Plaza, 9 Deer Park Drive, Suite C;Monmouth Junction, New Jersey, 08852 March 9, 2006
Recombinant fully human monoclonal antibody to anthrax protective antigen Anthrax PharmAthene, Inc.;One Park Place, Suite 450;Annapolis, Maryland, 21401 February 16, 2006
Clazosentan Cerebral vasospasm following subarachnoid hemorrhage Idorsia Pharmaceuticals US Inc.;1820 Chapel Avenue West, Suite 150;Cherry Hill, New Jersey, 08002 February 16, 2006
Nikkomycin Z Coccidioidomycosis Valley Fever Center for Excellence (1-111 INF);University of Arizona;Tucson, Arizona, 85723 February 14, 2006
Bevacizumab Ovarian cancer Genentech, Inc;1 DNA Way, M/S# 355E;South San Francisco, California, 94080 February 9, 2006
Solasonine and solamargine Metastatic Melanoma Solbec Pharmaceuticals Limited;P. O. Box 2142, Osbourne Park, Western Australia 6017; February 6, 2006
6,8-bis-benzylsulfanyl-octanoic acid Pancreatic Cancer Cornerstone Pharmaceuticals, Inc.;25 Health Science Drive;Stony Brook, New York, 11790 February 6, 2006
Blinatumomab Non-Hodgkin lymphoma Non-Hodgkin Lymphoma Amgen, Inc.;One Amgen Center Drive;Thousand Oaks, California February 6, 2006
N-acetyl-glucosamine thiazoline Adult Tay-Sachs disease ExSAR Corporation;11 Deer Park Drive;Monmouth Junction, New Jersey, 08852 February 6, 2006
Recombinant human alpha-mannosidase Alpha-mannosidosis Chiesi USA, Inc.;1255 Crescent Green, Suite 250;Cary, North Carolina, 27518 February 2, 2006
Aripiprazole Tourette syndrome Otsuka Pharmaceutical Development;and Commercialization, 1st Floor;Princeton, New Jersey, 08540 January 25, 2006
Recombinant anti-CD-40 monoclonal antibody Multiple myeloma Novartis Pharmaceutical Corporation;Oncology Business Unit, One Health Plaza, Bldg 104;East Hanover, New Jersey, 07936 January 25, 2006
Recombinant human microplasmin Peripheral arterial occlusion ThromboGenics Ltd;Unit 14, Bridgecourt Office Park;Dublin January 23, 2006
Iobenguane I 131 Neuroendocrine tumors Progenics Pharmaceuticals, Inc.;One World Trade Center., 47th Floor, Suite J;New York, New York, 10007 January 18, 2006
L-aminocarnityl-succinyl-leucyl-argininal-diethylacetal Duchenne muscular dystrophy CepTor Corporation;200 International Circle;Hunt Valley, Maryland, 21030 January 18, 2006
Fusion protein consisting of human immunoglobim G1 constant region Fc region fused to the human receptor binding domain of ectodysplasin-A1 X-linked Hypohidrotic Ectodermal Dysplasia Edimer Pharmaceuticals, Inc.;1 Broadway, 8th Floor;Cambridge, Massachusetts, 02142 January 11, 2006
Lentiviral vector encoded with a human beta-globin gene plasmid Beta-thalassemia Memorial Sloan-Kettering Cancer Center;1275 York Avenue, Box 65;New York, New York, 10065 January 11, 2006