Recombinant adeno-associated virus serotype 9 vector expressing codon-optimized miniaturized version of DMD gene

Recombinant adeno-associated virus serotype 9 vector expressing codon-optimized miniaturized version of DMD gene
Trade Name
Orphan Indication Duchenne muscular dystrophy
USA Market Approval USA
USA Designation Date 2017-05-22 00:00:00
Sponsor Bamboo Therapeutics, w wholly owned subsidiary of Pfizer;Worldwide Safety & Regulatory, Pfizer Inc.;Groton, Connecticut, 06340