an adeno-associated viral vector containing a codon-optimised human factor IX gene (AAV5-hFIXco) | |
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Trade Name | |
Orphan Indication | Hemophilia B |
USA Market Approval | USA |
USA Designation Date | 2011-12-22 00:00:00 |
Sponsor | uniQure, B.V.;Meiberdreef 61, 1100 DA;Amsterdam |