Adeno-associated viral vector differentially expressing microdystrophin 5 gene via the muscle-specific promoter CK8. | |
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Trade Name | |
Orphan Indication | Duchenne muscular dystrophy |
USA Market Approval | USA |
USA Designation Date | 2016-08-31 00:00:00 |
Sponsor | Solid GT, LLC;161 First Street, Suite 3A;Cambridge, Massachusetts, 02142 |