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generation 4 hydroxyl-terminated polyamidoamine dendrimer containing an ethylene diamine (EDA) core, amidoamine repate units, and 64 hydroxyl end groups |
|---|---|
| Trade Name | |
| Orphan Indication | X-linked adrenoleukodystrophy |
| USA Market Approval | USA |
| USA Designation Date | 2017-03-22 00:00:00 |
| Sponsor | Orpheris, Inc.;303 Twin Dolphin Drive, Suite 600;Redwood City, California, 94065 |
