|
adeno-associated viral vector serotype 9 containing the human cardiac calsequestrin gene |
|---|---|
| Trade Name | Calmarythm |
| Orphan Indication | Polymorphic Catecholergic Ventricular Tachycardia |
| USA Market Approval | USA |
| USA Designation Date | 2014-10-02 00:00:00 |
| Sponsor | Audentes Therapeutics, Inc.;101 Montgomery St., #2650;San Francisco, California, 94104 |
