 |
anti-sense oligonucleotide consisting of 2’0-Me RNA with a phosphorothioate backbone |
|---|---|
| Trade Name | |
| Orphan Indication | Cystic fibrosis |
| USA Market Approval | USA |
| USA Designation Date | 2013-09-23 00:00:00 |
| Sponsor | ProQR Therapeutics B.V.;Darwinweg 24, 2333 CR Leiden, The Netherlands; |
Related Access Program