|
adeno associated viral vector containing human ARSB gene |
|---|---|
| Trade Name | |
| Orphan Indication | Mucopolysaccharidosis type VI |
| USA Market Approval | USA |
| USA Designation Date | 2011-03-17 00:00:00 |
| Sponsor | Fondazione Telethon;Via Varese 16 - 00185 Roma; |
|
adeno associated viral vector containing human ARSB gene |
|---|---|
| Trade Name | |
| Orphan Indication | Mucopolysaccharidosis type VI |
| USA Market Approval | USA |
| USA Designation Date | 2011-03-17 00:00:00 |
| Sponsor | Fondazione Telethon;Via Varese 16 - 00185 Roma; |