 |
adeno-associated viral (AAV) vector serotype rh. 10 encoding the human N-sulfoglycosamine sulphohydrolase cDNA (SGSH) |
|---|---|
| Trade Name | |
| Orphan Indication | Sanfilippo Syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2015-11-18 00:00:00 |
| Sponsor | LYSOGENE;20 Rue Jacques Dulud;Neuilly-sur-Seine |
