 |
non-replicating recombinant adeno-associated viral vector, serotype 8, expressing the 1A1 isoform of the bilirubin-uridine diphosphate glucuronosyltransferase gene |
|---|---|
| Trade Name | |
| Orphan Indication | Crigler Najjar syndrome |
| USA Market Approval | USA |
| USA Designation Date | 2016-05-24 00:00:00 |
| Sponsor | Audentes Therapeutics, Inc.;600 California Street, 17th Floor;San Francisco, California, 94109 |
