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Recombinant adeno-associated viral vector serotype 2 carrying the gene for the human aromatic L-amino acid decarboxylase protein |
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| Trade Name | |
| Orphan Indication | Aromatic amino acid decarboxylase deficiency |
| EU Market Approval | EU |
| EU Designation Date | 2016-11-18 00:00:00 |
| Sponsor | Diamond BioPharm Limited |
