 |
antisense oligonucleotide complementary to the exonic splicer enhancer sequence at intron 26 of the centrosomal protein 290 pre-mRNA |
|---|---|
| Trade Name | |
| Orphan Indication | Leber's congenital amaurosis |
| USA Market Approval | USA |
| USA Designation Date | 2016-05-25 00:00:00 |
| Sponsor | ProQR Therapeutics IV B.V.;Zernikedreef 9, 2333 CK Leiden;Leiden |
