aadeno-associated viral vector, serotype 2, containing the human choroideremia gene encoding human Rab escort protein 1 | |
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Trade Name | |
Orphan Indication | Choroideremia |
USA Market Approval | USA |
USA Designation Date | 2013-09-12 00:00:00 |
Sponsor | Sparks Therapeutics, Inc.;3737 Market Street, Suite 1300;Philadelphia, Pennsylvania, 19104 |