modified mRNA encoding UGT1A1 protein, formulated in lipid nanoparticles | |
---|---|
Trade Name | |
Orphan Indication | Crigler-Najjar syndrome |
USA Market Approval | USA |
USA Designation Date | 2016-07-05 00:00:00 |
Sponsor | Moderna Therapeutics, Inc.;320 Bent Street;Cambridge, Massachusetts, 02141 |