adeno-associated viral vector serotype 2 containing the human Rab escort protein 1 gene | |
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Trade Name | |
Orphan Indication | Choroideremia |
USA Market Approval | USA |
USA Designation Date | 2014-11-05 00:00:00 |
Sponsor | NightstaRx Ltd.;215 Euston Road, NW1 2BE;London |