Recombinant AAV9 expressing human alpha-N-acetylglucosaminidase | |
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Trade Name | |
Orphan Indication | Mucopolysaccharidosis III-B (Sanfilippo Syndrome Type B) |
USA Market Approval | USA |
USA Designation Date | 2014-04-30 00:00:00 |
Sponsor | Abeona Therapeutics LLC;10000 Cedar Avenue;Cleveland, Ohio, 44106 |