Recombinant AAV9 expressing human alpha-N-acetylglucosaminidase

Recombinant AAV9 expressing human alpha-N-acetylglucosaminidase
Trade Name
Orphan Indication Mucopolysaccharidosis III-B (Sanfilippo Syndrome Type B)
USA Market Approval USA
USA Designation Date 2014-04-30 00:00:00
Sponsor Abeona Therapeutics LLC;10000 Cedar Avenue;Cleveland, Ohio, 44106