 |
adeno associated viral vector serotype rh.10 carrying the human SGSH and SUMF1 cDNAs |
|---|---|
| Trade Name | |
| Orphan Indication | Mucopolysaccharidosis type IIIA (Sanfilippo type A syndrome) |
| USA Market Approval | USA |
| USA Designation Date | 2013-05-06 00:00:00 |
| Sponsor | Lysogene;52 rue La Boetie;Paris |
