One, two, three, or four antisense oligonucleotides of Phosphorodiamidate morpholino oligomer combination that skips exons 4, 5, 6, and 7 of the gamma sarcoglycan (SGCG) gene | |
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Trade Name | |
Orphan Indication | Limb-girdle muscular dystrophy |
USA Market Approval | USA |
USA Designation Date | 2017-07-18 00:00:00 |
Sponsor | Kurt+Peter Foundation;P. O. Box 691;Menlo Park, California, 94025 |