|
adeno associated virus with modified transthyretin and sequence encoding factor IX variant gene |
|---|---|
| Trade Name | |
| Orphan Indication | Hemophilia B |
| USA Market Approval | USA |
| USA Designation Date | 2014-03-14 00:00:00 |
| Sponsor | Baxalta US, Inc.;One Baxter Way;Westlake Village, California, 91362 |
