adeno associated virus with modified transthyretin and sequence encoding factor IX variant gene | |
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Trade Name | |
Orphan Indication | Hemophilia B |
USA Market Approval | USA |
USA Designation Date | 2014-03-14 00:00:00 |
Sponsor | Baxalta US, Inc.;One Baxter Way;Westlake Village, California, 91362 |